Beyond Factor Replacement Therapy: New and Experimental Agents for Hemophilia

H&O  What are the limitations of factor VIII administration to prevent and treat bleeding in hemophilia? AV  Factor VIII administration entails frequent intravenous infusions, which require […]

Diagnosis and Treatment of Hemophilia

  Abstract: Hemophilia A and B are inherited bleeding disorders characterized by deficiency or dysfunction of coagulation protein factors VIII and IX, respectively. Recurrent joint and […]

Hem/Onc News

Recombinant Factor IX Approved for Use in Adults and Children With Hemophilia B The US Food and Drug Administration (FDA) approved the recombinant coagulation factor IX […]